MUT型甲基丙二酸血症基因治疗研究进展
丁一, 于玥, 韩连书
Research progress in gene therapy for MUT-type methylmalonic acidemia
Reviewer: DING Yi, YU Yue, Reviser: HAN Lianshu
临床儿科杂志 . 2024, (12): 1051 -1055 .  DOI: 10.12372/jcp.2024.24e0274